We found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitlePhase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector.AuthorsBowles DE; McPhee SW; Li C; Gray SJ; Samulski JJ; Camp AS; Li J; Wang B; Monahan PE; Rabinowitz JE; Grieger JC; Govindasamy L; Agbandje-McKenna M; Xiao X; Samulski RJPublicationMolecular therapy : the journal of the American Society of Gene Therapy, 2012, Vol 20, Issue 2, p443ISSN1525-0024Publication typearticleDOI10.1038/mt.2011.237