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Title
Preclinical PK and PD Studies on 2′-O-Methyl-phosphorothioate RNA Antisense Oligonucleotides in the mdx Mouse Model.
Authors
Heemskerk, Hans; de Winter, Christa; van Kuik, Petra; Heuvelmans, Niki; Sabatelli, Patrizia; Rimessi, Paola; Braghetta, Paola; van Ommen, Gert-Jan B.; de Kimpe, Sjef; Ferlini, Alessandra; Aartsma-Rus, Annemieke; van Deutekom, Judith C. T.