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Title
Correction of ADAMTS13 Deficiency by In Utero Gene Transfer of Lentiviral Vector encoding ADAMTS13 Genes.
Authors
Niiya, Masami; Endo, Masayuki; Dezhi Shang; Zoltick, Philip W; Muvarak, Nidal E.; Wenjing Cao; Sheng-Yu Jin; Skipwith, Christopher G.; Motto, David G.; Flake, Alan W.; Zheng, X. Long