We found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleLong-term observational, non-randomized study of enzyme replacement therapy in late-onset glycogenosis type II.AuthorsBembi, Bruno; Pisa, Federica; Confalonieri, Marco; Ciana, Giovanni; Fiumara, Agata; Parini, Rossella; Rigoldi, Miriam; Moglia, Arrigo; Costa, Alfredo; Carlucci, Annalisa; Danesino, Cesare; Pittis, Maria; Dardis, Andrea; Ravaglia, SabrinaPublicationJournal of Inherited Metabolic Disease, 2010, Vol 33, Issue 6, p727ISSN0141-8955Publication typearticleDOI10.1007/s10545-010-9201-8