We found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitlePTC124 targets genetic disorders caused by nonsense mutations.AuthorsWelch EM; Barton ER; Zhuo J; Tomizawa Y; Friesen WJ; Trifillis P; Paushkin S; Patel M; Trotta CR; Hwang S; Wilde RG; Karp G; Takasugi J; Chen G; Jones S; Ren H; Moon YC; Corson D; Turpoff AA; Campbell JA; Conn MM; Khan A; Almstead NG; Hedrick J; Mollin A; Risher N; Weetall M; Yeh S; Branstrom AA; Colacino JM; Babiak J; Ju WD; Hirawat S; Northcutt VJ; Miller LL; Spatrick P; He F; Kawana M; Feng H; Jacobson A; Peltz SW; Sweeney HLPublicationNature, 2007, Vol 447, Issue 7140, p87ISSN1476-4687Publication typearticleDOI10.1038/nature05756