We found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleGene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.AuthorsJacobson SG; Cideciyan AV; Ratnakaram R; Heon E; Schwartz SB; Roman AJ; Peden MC; Aleman TS; Boye SL; Sumaroka A; Conlon TJ; Calcedo R; Pang JJ; Erger KE; Olivares MB; Mullins CL; Swider M; Kaushal S; Feuer WJ; Iannaccone A; Fishman GA; Stone EM; Byrne BJ; Hauswirth WWPublicationArchives of ophthalmology (Chicago, Ill. : 1960), 2012, Vol 130, Issue 1, p9ISSN1538-3601Publication typearticleDOI10.1001/archophthalmol.2011.298