We found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleAAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival.AuthorsBaek RC; Broekman ML; Leroy SG; Tierney LA; Sandberg MA; d'Azzo A; Seyfried TN; Sena-Esteves MPublicationPloS one, 2010, Vol 5, Issue 10, pe13468ISSN1932-6203Publication typearticleDOI10.1371/journal.pone.0013468